Liver-Directed Gene Therapy for Hemophilia B with Immune Stealth Lentiviral Vectors
- Resource Type
- Abstract
- Authors
- Cantore, Alessio ; Milani, Michela ; Annoni, Andrea ; Liu, Tongyao ; Bartolaccini, Sara ; Biffi, Mauro ; Russo, Fabio ; Peters, Robert; Lombardo, Angelo ; Nichols, Timothy C.; Ayuso, Eduard ; Naldini, Luigi
- Source
- In Blood 8 December 2017 130 Supplement 1:605-605
- Subject
- Language
- ISSN
- 0006-4971