Lentiviral Gene Therapy with Autologous Hematopoietic Stem and Progenitor Cells (HSPCs) for the Treatment of Severe Combined Immune Deficiency Due to Adenosine Deaminase Deficiency (ADA-SCID): Results in an Expanded Cohort
Resource Type
Abstract
Authors
Kohn, Donald B. ; Shaw, Kit L. ; Garabedian, Elizabeth ; Carbonaro-Sarracino, Denise Ann ; Moore, Theodore B. ; De Oliveira, Satiro N. ; Crooks, Gay M. ; Tse, John ; Shupien, Sally ; Terrazas, Dayna ; Davila, Alejandra ; Icreverzi, Amalia ; Yu, Allen ; Chun, Krista M. ; Casas, Christian E. ; Barman, Provaboti ; Coronel, Maritess ; Campo Fernandez, Beatriz ; Zhang, Ruixue ; Hollis, Roger P. ; Uzowuru, Chilenwa ; Ricketts, Hilory ; Bayford, Jinhua Xu ; Trevisan, Valentina ; Arduini, Serena ; Lynn, Frances ; Kudari, Mahesh ; Spezzi, Andrea ; Reeves, Lilith ; Cornetta, Kenneth ; Sokolic, Robert A. ; Parrott, Roberta ; Buckley, Rebecca ; Booth, Claire ; Candotti, Fabio ; Malech, Harry L. ; Thrasher, Adrian J. ; Gaspar, H. Bobby
Source
In Blood 13 November 2019 134 Supplement 1:3345-3345
Subject
Language
ISSN
0006-4971