Vemurafenib for BRAF V600‐mutant Erdheim–Chester disease presenting with bilateral orbital involvement.
- Resource Type
- Case Study
- Authors
- Wang, Xiaomeng; Cao, Jie; Du, Weijiao; Ma, Wenchao; Meng, Bin; Cao, Shui
- Source
- Clinical Case Reports. Aug2023, Vol. 11 Issue 8, p1-6. 6p.
- Subject
- *ERDHEIM-Chester disease
*VEMURAFENIB
*THYROID eye disease
- Language
- ISSN
- 2050-0904
ECD is considered to have rapid progression and poor prognosis. Studies have shown that vemurafenib is effective for ECD patients with orbital involvement, but not for ECD with multiple organs. The refinement of treatment approaches and the increased awareness of ECD have led to a dramatic improvement in prognosis. [ABSTRACT FROM AUTHOR]