Nonclinical Safety Evaluation of scAAV8-RLBP1 for Treatment of RLBP1 Retinitis Pigmentosa
- Resource Type
- Journal
- Authors
- MacLachlan, Timothy K.; Milton, Mark N.; Turner, Oliver; Tukov, Francis; Choi, Vivian W.; Penraat, Jan; Hanks, Shawn M.; Vrouvlianis, Joanna; Leehy, Barrett; Li, Hui; Delmotte, Marie-Helene; Michaut, Lydia; Jaffee, Bruce D.; Bigelow, Chad E.
- Source
- MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT; MAR 2018, 8 p105-p120, 16p.
- Subject
- Language
- English
- ISSN
- 23290501