Human Molecular Genetics Jones, F E, Murray, L S, McNeilly, S, Dean, A, Aman, A, Lu, Y, Nikolova, N, Malomgré, R, Horsburgh, K, Holmes, W M, Kadler, K E & Van Agtmael, T 2019, ' 4-Sodium phenyl butyric acid has both efficacy and counter-indicative effects in the treatment of Col4a1 disease ', Human Molecular Genetics, vol. 28, no. 4, pp. 628-638 . https://doi.org/10.1093/hmg/ddy369 Jones, F E, Murray, L S, McNeilly, S, Dean, A, Aman, A, Lu, Y, Nikolova, N, Malomgré, R, Horsburgh, K, Holmes, W M, Kadler, K E & Van Agtmael, T 2018, ' 4-Sodium phenyl butyric acid has both efficacy and counter-indicative effects in the treatment of Col4a1 disease ', Human Molecular Genetics . https://doi.org/10.1093/hmg/ddy369