Orphanet Journal of Rare Diseases Orphanet Journal of Rare Diseases, Vol 13, Iss 1, Pp 1-11 (2018) Orphanet journal of rare diseases, 13(1):214. BioMed Central Orphanet Journal of Rare Diseases, 13(1):214. BioMed Central Schuller, Y, Biegstraaten, M, Hollak, C E M, Klümpen, H-J, Gispen-de Wied, C C & Stoyanova-Beninska, V 2018, ' Oncologic orphan drugs approved in the EU-Do clinical trial data correspond with real-world effectiveness? ', Orphanet Journal of Rare Diseases, vol. 13, no. 1, 214 . https://doi.org/10.1186/s13023-018-0900-9
Weinreich, S S, Vrinten, C, Kuijpers, M R, Lipka, A F, Schimmel, K J M, Van Zwet, E W, Gispen-De Wied, C, Hekster, Y A, Verschuuren, J J G M & Cornel, M C 2017, ' Aggregated N-of-1 trials for unlicensed medicines for small populations : an assessment of a trial with ephedrine for myasthenia gravis ', Orphanet Journal of Rare Diseases, vol. 12, no. 1, 88 . https://doi.org/10.1186/s13023-017-0636-y Orphanet Journal of Rare Diseases, Vol 12, Iss 1, Pp 1-18 (2017) Orphanet Journal of Rare Diseases Orphanet Journal of Rare Diseases, 12(1):88. BioMed Central Orphanet Journal of Rare Diseases, 12