Risdiplam treatment has not led to retinal toxicity in patients with spinal muscular atrophy
- Resource Type
- Journal
- Authors
- Sergott, Robert C.; Amorelli, Giulia M.; Baranello, Giovanni; Barreau, Emmanuel; Beres, Shannon; Kane, Steven; Mercuri, Eugenio; Orazi, Lorenzo; SantaMaria, Melissa; Tremolada, Gemma; Santarsiero, Diletta; Waskowska, Agnieszka; Yashiro, Shigeko; Denk, Nora; Furst-Recktenwald, Sabine; Gerber, Marianne; Gorni, Ksenija; Jaber, Birgit; Jacobsen, Bjoern; Mueller, Lutz; Nave, Stephane; Scalco, Renata S.; Marzoli, Stefania B.; FIREFISH Working Grp; SUNFISH Working Grp; Jewelfish Working Grp
- Source
- ANNALS OF CLINICAL AND TRANSLATIONAL NEUROLOGY; NOV 24 2020, 12p.
- Subject
- Language
- English
- ISSN
- 23289503