Sustained Correction of a Murine Model of Phenylketonuria following a Single Intravenous Administration of AAVHSC15-PAH
- Resource Type
- Journal
- Authors
- Ahmed, Seemin S.; Rubin, Hillard; Wang, Minglun; Faulkner, Deiby; Sengooba, Arnold; Dollive, Serena N.; Avila, Nancy; Ellsworth, Jeff L.; Lamppu, Diana; Lobikin, Maria; Lotterhand, Jason; Adamson-Small, Laura; Wright, Teresa; Seymour, Albert; Francone, Omar L.
- Source
- MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT; JUN 12 2020, 17 p568-p580, 13p.
- Subject
- Language
- English
- ISSN
- 23290501