Treatment Efficiency in Gaucher Patients Can Reliably Be Monitored by Quantification of Lyso-Gb1 Concentrations in Dried Blood Spots
- Resource Type
- Journal
- Authors
- Cozma, Claudia; Cullufi, Paskal; Kramp, Guido; Hovakimyan, Marina; Velmishi, Virtut; Gjikopulli, Agim; Tomori, Sonila; Fischer, Steffen; Oppermann, Sebastian; Grittner, Ulrike; Bauer, Peter; Beetz, Christian; Rolfs, Arndt
- Source
- INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES; JUL 2020, 21 13, p4577 9p.
- Subject
- Language
- English
- ISSN
- 14220067