High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia
- Resource Type
- Journal
- Authors
- Vaidyanathan, Sriram; Salahudeen, Ameen A.; Sellers, Zachary M.; Bravo, Dawn T.; Choi, Shannon S.; Batish, Arpit; Le, Wei; Baik, Ron; de la O, Sean; Kaushik, Milan P.; Galper, Noah; Lee, Ciaran M.; Teran, Christopher A.; Yoo, Jessica H.; Bao, Gang; Chang, Eugene H.; Patel, Zara M.; Hwang, Peter H.; Wine, Jeffrey J.; Milla, Carlos E.; Desai, Tushar J.; Nayak, Jayakar, V; Kuo, Calvin J.; Porteus, Matthew H.
- Source
- CELL STEM CELL; FEB 6 2020, 26 2, p161-p+, 15p.
- Subject
- Language
- English
- ISSN
- 18759777