A RUNX1-FPDMM rhesus macaque model reproduces the human phenotype and predicts challenges to curative gene therapies
- Resource Type
- Short Communication
- Authors
- Lee, Byung-Chul ; Zhou, Yifan ; Bresciani, Erica; Ozkaya, Neval; Dulau-Florea, Alina; Carrington, Blake; Shin, Tae-Hoon; Baena, Valentina; Syed, Zulfeqhar A.; Hong, So Gun; Zhen, Tao; Calvo, Katherine R.; Liu, Paul ; Dunbar, Cynthia E.
- Source
- In Blood October 2022
- Subject
- Gene Therapy
- Language
- ISSN
- 0006-4971