P.51 Real-world experience after one year treating SMA children with risdiplam
- Resource Type
- Abstract
- Authors
- de la Banda, M. Gomez Garcia; Garcia-Uzquiano, R.; Benezit, A.; Davion, J.; Dabaj, I.; Amthor, H.; Bouadi, A.; Spigarelli, M.; Bocassin, C.; Tirolien, S.; Villart, M.; Sonnet, L.; Grimaldi-Bensouda, L.; Quijano-Roy, S.
- Source
- In Neuromuscular Disorders October 2022 32 Supplement 1:S62-S62
- Subject
- Language
- ISSN
- 0960-8966