COMET post hoc analysis: Efficacy of long-term avalglucosidase alfa in subgroups of participants with late-onset Pompe disease
- Resource Type
- Abstract
- Authors
- Toscano, Antonio; Kishnani, Priya; Dimachkie, Mazen M.; Sacconi, Sabrina; Van der Beek, Nadine; Roberts, Mark E.; Suwazono, Shugo; Choi, Young Chul; de Souza, Paulo Victor Sgobbi; Schoser, Benedikt; Armstrong, Nicole; Huynh-Ba, Olivier; Thibault, Nathan; Periquet, Magali; Diaz-Manera, Jordi
- Source
- In Molecular Genetics and Metabolism February 2024 141(2)
- Subject
- Language
- ISSN
- 1096-7192