Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial
Resource Type
Article
Authors
Castaman, Giancarlo ; Crary, Shelley E ; Escobar, Miguel ; Gomez, Esteban ; Haley, Kristina M ; Hermans, Cedric R J R ; Kampmann, Peter ; Kazmi, Rashid ; Key, Nigel S ; Klamroth, Robert ; Konkle, Barbara A ; Kruse-Jarres, Rebecca ; Lattimore, Susan ; Lemons, Richard ; Meijer, Karina ; O'Connell, Niamh ; Quon, Doris V ; Raheja, Priyanka ; Symington, Emily ; Verhamme, Peter ; Visweshwar, Nathan ; von Drygalski, Annette ; Wang, Michael ; Wheeler, Allison P ; White, Shanna ; Young, Guy ; Coppens, Michiel ; Pipe, Steven W ; Miesbach, Wolfgang ; Astermark, Jan ; Recht, Michael ; van der Valk, Paul ; Ewenstein, Bruce ; Pinachyan, Karen ; Galante, Nicholas ; Le Quellec, Sandra ; Monahan, Paul E ; Leebeek, Frank W G
Source
In The Lancet Haematology April 2024 11(4):e265-e275
Subject
Primary Research Articles
Language
ISSN
2352-3026