FollowME Fabry Pathfinders Registry: Renal effectiveness in a cohort of patients on migalastat treatment for at least three years
- Resource Type
- Abstract
- Authors
- West, Michael L.; Hughes, Derralynn; Sunder-Plassmann, Gere; Jovanovic, Ana; Brand, Eva; Bichet, Daniel G.; Pisani, Antonio; Nowak, Albina; Torra, Roser; Khan, Aneal; Azevedo, Olga; Lehman, Anna; Linhart, Aleš; Rutecki, Jasmine; Giuliano, Joseph D.; Krusinska, Eva; Nordbeck, Peter
- Source
- In Molecular Genetics and Metabolism February 2024 141(2)
- Subject
- Language
- ISSN
- 1096-7192