Multiplex CRISPR/Cas9 Genome Editing Targeting the BCL11A/HBG Axis Maximizes Fetal Hemoglobin Reinduction but Generates Chromosomal Translocations Which Persist In Vivo
- Resource Type
- Abstract
- Source
- In
Blood 5 November 2020 136 Supplement 1:47-48 - Subject
- Language
- ISSN
- 0006-4971