Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study
Resource Type
Article
Authors
Ferrua, Francesca ; Cicalese, Maria Pia ; Galimberti, Stefania ; Giannelli, Stefania ; Dionisio, Francesca ; Barzaghi, Federica ; Migliavacca, Maddalena ; Bernardo, Maria Ester ; Calbi, Valeria ; Assanelli, Andrea Angelo ; Facchini, Marcella ; Fossati, Claudia ; Albertazzi, Elena ; Scaramuzza, Samantha ; Brigida, Immacolata ; Scala, Serena ; Basso-Ricci, Luca ; Pajno, Roberta ; Casiraghi, Miriam ; Canarutto, Daniele ; Salerio, Federica Andrea ; Albert, Michael H ; Bartoli, Antonella ; Wolf, Hermann M ; Fiori, Rossana ; Silvani, Paolo ; Gattillo, Salvatore ; Villa, Anna ; Biasco, Luca ; Dott, Christopher ; Culme-Seymour, Emily J ; van Rossem, Koenraad ; Atkinson, Gillian ; Valsecchi, Maria Grazia ; Roncarolo, Maria Grazia ; Ciceri, Fabio ; Naldini, Luigi ; Aiuti, Alessandro
Source
In The Lancet Haematology May 2019 6(5):e239-e253
Subject
Primary Research Articles
Language
ISSN
2352-3026