Efficacy and Safety of a Single Dose of Exagamglogene Autotemcel for Severe Sickle Cell Disease
- Resource Type
- Abstract
- Authors
- Frangoul, Haydar; Locatelli, Franco; Bhatia, Monica ; Mapara, Markus Y.; Molinari, Lyndsay ; Sharma, Akshay; Lobitz, Stephan ; de Montalembert, Mariane; Rondelli, Damiano; Steinberg, Martin; Walters, Mark C.; Imren, Suzan ; Zhang, Lanju ; Sharma, Anjali ; Song, Yang ; Simard, Christopher ; Hobbs, William ; Grupp, Stephen
- Source
- In Blood 15 November 2022 140 Supplement 1:29-31
- Subject
- Language
- ISSN
- 0006-4971