Genome editing of HBG1 and HBG2 to induce fetal hemoglobin
- Resource Type
- Article
- Authors
- Métais, Jean-Yves ; Doerfler, Phillip A. ; Mayuranathan, Thiyagaraj ; Bauer, Daniel E.; Fowler, Stephanie C.; Hsieh, Matthew M.; Katta, Varun; Keriwala, Sagar; Lazzarotto, Cicera R.; Luk, Kevin; Neel, Michael D.; Perry, S. Scott; Peters, Samuel T.; Porter, Shaina N.; Ryu, Byoung Y.; Sharma, Akshay; Shea, Devlin; Tisdale, John F.; Uchida, Naoya; Wolfe, Scot A.; Woodard, Kaitly J.; Wu, Yuxuan; Yao, Yu; Zeng, Jing; Pruett-Miller, Shondra; Tsai, Shengdar Q.; Weiss, Mitchell J.
- Source
- In Blood Advances 12 November 2019 3(21):3379-3392
- Subject
- Language
- ISSN
- 2473-9529