Severe CNS involvement in a subset of long-term treated children with infantile-onset Pompe disease
- Resource Type
- Article
- Authors
- Kenney-Jung, Daniel; Korlimarla, Aditi; Spiridigliozzi, Gail A.; Wiggins, Walter; Malinzak, Michael; Nichting, Gretchen; Jung, Seung-Hye; Sun, Angela; Wang, Raymond Y.; Al Shamsi, Aisha; Phornphutkul, Chanika; Owens, James; Provenzale, James M.; Kishnani, Priya S.
- Source
- In Molecular Genetics and Metabolism February 2024 141(2)
- Subject
- Language
- ISSN
- 1096-7192