Antisense oligonucleotide-based drug development for Cystic Fibrosis patients carrying the 3849+10 kb C-to-T splicing mutation
- Resource Type
- Article
- Authors
- Oren, Yifat S.; Irony-Tur Sinai, Michal; Golec, Anita; Barchad-Avitzur, Ofra; Mutyam, Venkateshwar; Li, Yao; Hong, Jeong; Ozeri-Galai, Efrat; Hatton, Aurélie; Leibson, Chen; Carmel, Liran; Reiter, Joel; Sorscher, Eric J.; Wilton, Steve D.; Kerem, Eitan; Rowe, Steven M.; Sermet-Gaudelus, Isabelle; Kerem, Batsheva
- Source
- In Journal of Cystic Fibrosis September 2021 20(5):865-875
- Subject
- Language
- ISSN
- 1569-1993