Evaluating the efficacy and safety of pozelimab in patients with CD55 deficiency with hyperactivation of complement, angiopathic thrombosis, and protein-losing enteropathy disease: an open-label phase 2 and 3 study
Resource Type
Article
Authors
Miller, Jutta L. ; Eshach Adiv, Orly ; Bilgic Eltan, Sevgi ; Yorgun Altunbas, Melek ; Magliocco, Mary ; Matthews, Helen ; Marciano, Beatriz E. ; Chatchatee, Pantipa ; Trbovic, Caryn F. ; Burczynski, Michael E. ; Chaudhari, Umesh ; Usta, Yusuf ; Altuntaş, Cansu ; Yavuz, Sibel ; Baştürk, Ahmet ; Demirbaş Ar, Fatma ; Topal, Erdem ; Kalaycı, Ayhan Gazi ; Weerapakorn, Wanlapa ; Calabi Martínez, Ana Andrea ; Bottero, Adriana ; Ozen, Ahmet ; Chongsrisawat, Voranush ; Sefer, Asena Pinar ; Kolukisa, Burcu ; Jalbert, Jessica J ; Meagher, Karoline A ; Brackin, Taylor ; Feldman, Hagit Baris ; Baris, Safa ; Karakoc-Aydiner, Elif ; Ergelen, Rabia ; Fuss, Ivan J ; Moorman, Heather ; Suratannon, Narissara ; Suphapeetiporn, Kanya ; Perlee, Lorah ; Harari, Olivier A ; Yancopoulos, George D ; Lenardo, Michael J
Source
In The Lancet 17-23 February 2024 403(10427):645-656
Subject
Primary Research Articles
Language
ISSN
0140-6736