Pegvaliase for the treatment of phenylketonuria: Final results of a long-term phase 3 clinical trial program
- Resource Type
- Article
- Authors
- Harding, Cary O.; Longo, Nicola; Northrup, Hope; Sacharow, Stephanie; Singh, Rani; Thomas, Janet A.; Vockley, Jerry; Zori, Roberto T.; Bulloch Whitehall, Kaleigh; Lilienstein, Joshua; Lindstrom, Kristin; Levy, Drew G.; Jones, Shaun; Burton, Barbara K.
- Source
- In Molecular Genetics and Metabolism Reports June 2024 39
- Subject
- Language
- ISSN
- 2214-4269