Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial
- Resource Type
- Article
- Authors
- Glenthøj, Andreas ; van Beers, Eduard J; Al-Samkari, Hanny; Viprakasit, Vip; Kuo, Kevin H M; Galactéros, Frédéric; Chonat, Satheesh; Porter, John; Zagadailov, Erin; Xu, Rengyi; Oluyadi, Abdulafeez; Hawkins, Peter; Gheuens, Sarah; Beynon, Vanessa; Barcellini, Wilma
- Source
- In The Lancet Haematology October 2022 9(10):e724-e732
- Subject
- Primary Research
Articles
- Language
- ISSN
- 2352-3026