Fatal thrombotic microangiopathy case following adeno-associated viral SMN gene therapy
- Resource Type
- Article
- Authors
- Guillou, Julia ; de Pellegars, Alice ; Porcheret, Florence; Frémeaux-Bacchi, Véronique; Allain-Launay, Emma; Debord, Camille; Denis, Manon; Péréon, Yann; Barnérias, Christine; Desguerre, Isabelle ; Roussey, Gwenaëlle ; Mercier, Sandra
- Source
- In Blood Advances 26 July 2022 6(14):4266-4270
- Subject
- Language
- ISSN
- 2473-9529