Validation of GMFC-MLD scale as a measure of gross motor function in metachromatic leukodystrophy
- Resource Type
- Abstract
- Authors
- Mutua, Sylvia; Sevagamoorthy, Anjana; Gavazzi, Francesco; Thakur, Nivedita; Woidill, Sarah; Yu, Emily; Fumagalli, Francesca; Groeschel, Samuel; Bernard, Genevieve; Stutterd, Chloe; Kehrer, Christiane; Emrick, Lisa; Shults, Justine; Vanderver, Adeline; Adang, Laura A.
- Source
- In Molecular Genetics and Metabolism February 2024 141(2)
- Subject
- Language
- ISSN
- 1096-7192