Efficacy and safety of once-daily nitisinone for patients with alkaptonuria (SONIA 2): an international, multicentre, open-label, randomised controlled trial
Resource Type
Article
Authors
Ranganath, Lakshminarayan R ; Psarelli, Eftychia Eirini ; Arnoux, Jean-Baptiste ; Braconi, Daniela ; Briggs, Michael ; Bröijersén, Anders ; Loftus, Nadia ; Bygott, Helen ; Cox, Trevor F ; Davison, Andrew S ; Dillon, Jane P ; Fisher, Michael ; FitzGerald, Richard ; Genovese, Federica ; Glasova, Helena ; Hall, Anthony K ; Hughes, Andrew T ; Hughes, Juliette H ; Imrich, Richard ; Jarvis, Jonathan C ; Khedr, Milad ; Laan, Dinny ; Le Quan Sang, Kim-Hanh ; Luangrath, Emily ; Lukáčová, Ol'ga ; Milan, Anna M ; Mistry, Alpesh ; Mlynáriková, Vanda ; Norman, Brendan P ; Olsson, Birgitta ; Rhodes, Nicholas P ; Rovenský, Jozef ; Rudebeck, Mattias ; Santucci, Annalisa ; Shweihdi, Ella ; Scott, Ciarán ; Sedláková, Jana ; Sireau, Nicolas ; Stančík, Roman ; Szamosi, Johan ; Taylor, Sophie ; van Kan, Christa ; Vinjamuri, Sobhan ; Vrtíková, Eva ; Webb, Chris ; West, Elizabeth ; Záňová, Elizabeth ; Zatkova, Andrea ; Gallagher, James A
Source
In The Lancet Diabetes & Endocrinology September 2020 8(9):762-772
Subject
Primary Research Articles
Language
ISSN
2213-8587