Improved Gene Therapy for Metachromatic Leukodystrophy
- Resource Type
- Abstract
- Authors
- Tricoli, Lucas; Vanderver, Adeline; Adang, Laura; Chappell, Maxwell; Breda, Laura; Tanaka, Naoto; Triebwasser, Michael; Wenger, David; Jarocha, Danuta Jadwiga; Guerra, Amaliris; Schlotawa, Lars; Radhakrishnan, Karthikeyan; Ahrens-Nicklas, Rebecca; Kurre, Peter; Hurwitz, Stephanie; Rivella, Stefano
- Source
- In Blood 23 November 2021 138 Supplement 1:3979-3979
- Subject
- Language
- ISSN
- 0006-4971