Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1
- Resource Type
- Article
- Authors
- O’Mahony, Brian; Dunn, Amy L.; Leavitt, Andrew D.; Peyvandi, Flora; Ozelo, Margareth C.; Mahlangu, Johnny; Peerlinck, Kathelijne; Wang, Jiaan-Der; Lowe, Gillian C.; Tan, Chee Wee; Giermasz, Adam; Tran, Huyen; Khoo, Teh-Liane; Cockrell, Erin; Pepperell, Dominic; Chambost, Hervé; López Fernández, Maria Fernanda; Kazmi, Rashid; Majerus, Elaine; Skinner, Mark W.; Klamroth, Robert; Quinn, Jennifer; Yu, Hua; Wong, Wing Yen; Robinson, Tara M.; Pipe, Steven W.
- Source
- In Journal of Thrombosis and Haemostasis December 2023 21(12):3450-3462
- Subject
- Language
- ISSN
- 1538-7836