Stable and durable factor IX levels in patients with hemophilia B over 3 years after etranacogene dezaparvovec gene therapy
- Resource Type
- Article
- Authors
- von Drygalski, Annette; Gomez, Esteban; Giermasz, Adam; Castaman, Giancarlo; Key, Nigel S.; Lattimore, Susan U.; Leebeek, Frank W. G.; Miesbach, Wolfgang A.; Recht, Michael; Gut, Robert; Dolmetsch, Ricardo; Monahan, Paul E.; Le Quellec, Sandra; Pipe, Steven W.
- Source
- In Blood Advances 10 October 2023 7(19):5671-5679
- Subject
- Gene Therapy
Clinical Trials and Observations
- Language
- ISSN
- 2473-9529