Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial
Resource Type
Article
Authors
Sessa, Maria ; Lorioli, Laura ; Fumagalli, Francesca ; Acquati, Serena ; Redaelli, Daniela ; Baldoli, Cristina ; Canale, Sabrina ; Lopez, Ignazio D ; Morena, Francesco ; Calabria, Andrea ; Fiori, Rossana ; Silvani, Paolo ; Rancoita, Paola M V ; Gabaldo, Michela ; Benedicenti, Fabrizio ; Antonioli, Gigliola ; Assanelli, Andrea ; Cicalese, Maria Pia ; del Carro, Ubaldo ; Sora, Maria Grazia Natali ; Martino, Sabata ; Quattrini, Angelo ; Montini, Eugenio ; Di Serio, Clelia ; Ciceri, Fabio ; Roncarolo, Maria Grazia ; Aiuti, Alessandro ; Naldini, Luigi ; Biffi, Alessandra
Source
In The Lancet 30 July-5 August 2016 388(10043):476-487
Subject
Primary Research Articles
Language
ISSN
0140-6736