Enzyme replacement therapy rate escalation in infantile onset Pompe disease
- Resource Type
- Source
- Molecular Genetics and Metabolism. 117:S119
- Subject
Pediatrics medicine.medical_specialty Endocrinology business.industry Endocrinology, Diabetes and Metabolism Genetics medicine Enzyme replacement therapy Disease Infantile onset business Molecular Biology Biochemistry - Language
- ISSN
- 1096-7192