Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy
- Resource Type
- Source
- Bone Marrow Transplantation
- Subject
0301 basic medicine Male medicine.medical_specialty Transplantation Conditioning medicine.medical_treatment Genetic enhancement Twins Hematopoietic stem cell transplantation Hematology Transplantation, ARSA, Gene Therapy Defibrotide 03 medical and health sciences 0302 clinical medicine Polydeoxyribonucleotides Internal medicine Correspondence medicine Humans Transplantation business.industry Hematopoietic Stem Cell Transplantation Hematopoietic stem cell Genetic Therapy Leukodystrophy, Metachromatic Gene Therapy medicine.disease Metachromatic leukodystrophy 030104 developmental biology medicine.anatomical_structure 030220 oncology & carcinogenesis Immunology Platelet aggregation inhibitor ARSA business Platelet Aggregation Inhibitors medicine.drug - Language
- English