Efficient Correction of ELANE mutations in Primary HSPCs of Severe Congenital Neutropenia Patients Using CRISPR/Cas9 and rAVV6 HDR Repair Templates
- Resource Type
- Article
- Authors
- Ritter, Malte U; Secker, Benjamin; Klimiankou, Maksim; Nasri, Masoud; Aghaallaei, Narges; Dannenmann, Benjamin; Bernhard, Regine; Steiert, Ingeborg; Haehnel, Karin; Bajoghli, Baubak; Zeidler, Cornelia; Welte, Karl; Skokowa, Julia
- Source
- Blood; November 2019, Vol. 134 Issue: Supplement 1 p1036-1036, 1p
- Subject
- Language
- ISSN
- 00064971; 15280020
No relevant conflicts of interest to declare.