eP230 - HMI-203: Gene therapy developmental candidate for mucopolysaccharidosis type II (MPS II), or Hunter syndrome.
- Resource Type
- Article
- Authors
- Patel, Kruti; Smith, Laura; Seabrook, Tania; Tzianabos, Alec; Schulman, Lindsay; Zhivivh, Victor; Kivaa, Monicah; Faulkner, Deiby; Sengooba, Arnold; Behmoiras, Liana; Newman, Jennifer; Dollive, Serena; Avila, Nancy; Zhao, Jingyan; White, Yvonne; Woodcock, Steve; Smith, Sean; Francone, Omar; Gingras, Jacinthe; Seymour, Albert
- Source
- Molecular Genetics & Metabolism. 2021 Supplement 1, Vol. 132, pS147-S147. 1p.
- Subject
- *GENE therapy
*MUCOPOLYSACCHARIDOSIS
*SYNDROMES
*HUNTERS
- Language
- ISSN
- 1096-7192