Preventing Fabry disease progression in a symptomatic mouse model with a recombinant adeno-associated virus (rAAV) based gene therapy.
- Resource Type
- Article
- Authors
- Islam, Rizwana; Boukharov, Natalia; Chen, Nancy; Dasari, Bhanu; Mukherjee, Durba; Mukherji, Shreya; Park, Eric; Rompikuntal, Pramod; Ruangsiriluk, Wanida; Steinkellner, Julia; Wiseman, Jennifer; Yuan, Shipeng; Deshpande, Mugdha
- Source
- Molecular Genetics & Metabolism. Feb2023, Vol. 138 Issue 2, pN.PAG-N.PAG. 1p.
- Subject
- *ANGIOKERATOMA corporis diffusum
*ADENO-associated virus
*RECOMBINANT viruses
*GENE therapy
*LABORATORY mice
*MICE
- Language
- ISSN
- 1096-7192