Systemic Gene Transfer with rAAVrh74.MHCK7.SGCB Increased -sarcoglycan Expression in Patients with Limb Girdle Muscular Dystrophy Type 2E.
- Resource Type
- Article
- Authors
- Rodino-Klapac, Louise; Pozsgai, Eric; Lewis, Sarah; Griffin, Danielle; Meadows, Aaron; Lehman, Kelly; Church, Kathleen; Miller, Natalie; Iammarino, Megan; Lowes, Linda; Mendell, Jerry
- Source
- Neuropediatrics. 2019 Supplement2, Vol. 50, pS1-S55. 55p.
- Subject
- *GENETIC transformation
*MUSCULAR dystrophy
*CREATINE kinase
*MUSCLE weakness
*LIVER enzymes
- Language
- ISSN
- 0174-304X