Enzyme replacement therapy with recombinant pro-CTSD (cathepsin D) corrects defective proteolysis and autophagy in neuronal ceroid lipofuscinosis.
- Resource Type
- Article
- Authors
- Marques, André R. A.; Di Spiezio, Alessandro; Thießen, Niklas; Schmidt, Lina; Grötzinger, Joachim; Lüllmann-Rauch, Renate; Damme, Markus; Storck, Steffen E.; Pietrzik, Claus U.; Fogh, Jens; Bär, Julia; Mikhaylova, Marina; Glatzel, Markus; Bassal, Mahmoud; Bartsch, Udo; Saftig, Paul
- Source
- Autophagy. May2020, Vol. 16 Issue 5, p811-825. 15p.
- Subject
- Language
- ISSN
- 1554-8627