Rapid disease progression after enzyme replacement therapy interruption in a patient with cholesteryl ester storage disorder.
- Resource Type
- Article
- Source
Molecular Genetics & Metabolism . Feb2023, Vol. 138 Issue 2, pN.PAG-N.PAG. 1p.- Subject
- *
ENZYME replacement therapy
*DISEASE progression
*ESTERS
*STORAGE - Language
- ISSN
- 1096-7192