Gene therapy for cross-correction of somatic organs and the CNS in mucopolysaccharidosis II in rodents and non-human primates
- Resource Type
- Article
- Authors
- Chen, Nancy; Ehmann, David E.; Crooker, Robert; Derakhchan, Katayoun; Fang, Xiaodong; Felice, Brian; Galbreath, Elizabeth J.; Glaus, Charles; Gu, Hongbo; Huang, Yan; Li, Christine; Li, Xing; Liu, Nan; Palmieri, Kathleen; Simic, Damir; Sypek, Joseph; Thompson, Susan; Winkelmann, Christopher T.; Choi, Vivian W.
- Source
- In Molecular Therapy - Methods & Clinical Development 8 June 2023 29:286-302
- Subject
- Language
- ISSN
- 2329-0501