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1 . Academic Journal
342 Comparison of rectal organoid and clinical responses to modulators in people with CF homozygous for F508del-CFTR.
저자
by
Mier, N. Rodriguez
;
Ramalho, A.S.
;
De Wachter, E.
;
van Biervliet, S.
;
Lequesne, M.
, et al.
소스
Journal of Cystic Fibrosis
. Sep2024 Supplement 2, Vol. 23, pS180-S181. 2p.
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7 . Academic Journal
271 Prime editing functionally corrects rare and common cystic fibrosis–causing mutations in patient-derived organoids and airway epithelia.
저자
by
Bulcaen, M.
;
Kortleven, P.
;
Liu, R.
;
Maule, G.
;
Dreano, E.
, et al.
소스
Journal of Cystic Fibrosis
. Sep2024 Supplement 2, Vol. 23, pS144-S145. 2p.
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7 . Academic Journal
P071 Evaluation of CFTR modulator efficacy by rectal organoid morphology analysis (ROMA) indexes
저자
by
Cuyx, S.
;
Ramalho, A.S.
;
Proesmans, M.
;
Boon, M.
;
Dupont, L.
, et al.
소스
In
Journal of Cystic Fibrosis
June 2023 22 Supplement 2:S85-S85
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7 . Academic Journal
WS09.02 Theratyping molecular defects of CFTR rare variants in patient derived rectal organoids
저자
by
Soeffers, Y.
;
Cuyx, S.
;
Proesmans, M.
;
Dupont, L.
;
Van Hoorenbeeck, K.
, et al.
소스
In
Journal of Cystic Fibrosis
June 2023 22 Supplement 2:S18-S18
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7 . Academic Journal
WS04.06 Validation of rectal organoid morphology analysis (ROMA) as a novel physiological CFTR assay for diagnosis of cystic fibrosis
저자
by
Cuyx, S.
;
Ramalho, A.S.
;
Proesmans, M.
;
Boon, M.
;
Dupont, L.
, et al.
소스
In
Journal of Cystic Fibrosis
June 2023 22 Supplement 2:S9-S9
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7 . Academic Journal
WS16.02 Base editing strategy to repair the CFTR 2789 + 5G > A splicing mutation
저자
by
Amistadi, S.
;
Maule, G.
;
Ensinck, M.
;
De Keersmaecker, L.
;
Guidone, D.
, et al.
소스
In
Journal of Cystic Fibrosis
June 2022 21 Supplement 1:S31-S31
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7 . Academic Journal
WS16.01 Correction of the drug-refractory CFTR mutation L227R by prime editing
저자
by
Bulcaen, M.
;
Ensinck, M.M.
;
De Keersmaecker, L.
;
Maule, G.
;
Ramalho, A.S.
, et al.
소스
In
Journal of Cystic Fibrosis
June 2022 21 Supplement 1:S30-S31
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7 . Academic Journal
WS06.03 Novel CFTR modulator combinations maximise functional rescue of G85E and N1303K in rectal organoids
저자
by
Ensinck, M.M.
;
De Keersmaecker, L.
;
Ramalho, A.S.
;
Cuyx, S.
;
Van Biervliet, S.
, et al.
소스
In
Journal of Cystic Fibrosis
June 2022 21 Supplement 1:S12-S12
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7 . Academic Journal
341 Targeting elexacaftor/tezacaftor/ivacaftor-unresponsive CFTRmutations: novel drug combos in patient-derived organoids.
저자
by
Ramalho, A.S.
;
Mier, N.
;
Boon, M.
;
Dupont, L.
;
De Boeck, K.
, et al.
소스
Journal of Cystic Fibrosis
. Sep2024 Supplement 2, Vol. 23, pS180-S180. 1p.
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7 . Academic Journal
318 Investigation of CFTR function and epithelial barrier properties at single-cell resolution using multi-electrode array technology.
저자
by
Ensinck, M.
;
Venz, A.
;
Ramalho, A.S.
;
Takalloo, S. Ebrahimi
;
Vermeulen, F.
, et al.
소스
Journal of Cystic Fibrosis
. Sep2024 Supplement 2, Vol. 23, pS169-S169. 1p.
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