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1 . Academic Journal
AAV mediated gene therapy for haemophilia B: From the early attempts to modern trials
저자
by
Muczynski, Vincent
;
Nathwani, Amit C.
.
소스
In
Thrombosis Research
April 2024 236:242-249
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4 . Academic Journal
Mathematical modelling of gene delivery in patients with haemophilia B
저자
by
Jamili, Elnaz
;
Nathwani, Amit C.
;
Dua, Vivek
.
소스
In
Chemical Engineering Science
5 November 2023 281
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5 . Academic Journal
Transplacental delivery of therapeutic proteins by engineered immunoglobulin G: a step toward perinatal replacement therapy
저자
by
Mimoun, Angelina
;
Bou-Jaoudeh, Melissa
;
Delignat, Sandrine
;
Daventure, Victoria
;
Reyes Ruiz, Alejandra
, et al.
소스
In
Journal of Thrombosis and Haemostasis
September 2023 21(9):2405-2417
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7 . Academic Journal
Differences in wild-type– and R338L-tenase complex formation are at the root of R338L-factor IX assay discrepancies
저자
by
Foley, Jonathan H.
;
Shehu, Erald
;
Riddell, Anne
;
Gray, Elaine
;
Goodale, Andrew
, et al.
소스
In
Blood Advances
14 February 2023 7(3):458-467
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7 . Academic Journal
Pre-Existing Immunity to a Nucleic Acid Contaminant-Derived Antigen Mediates Transaminitis and Resultant Diminished Transgene Expression in a Mouse Model of Hepatic Recombinant Adeno-Associated Virus-Mediated Gene Transfer.
저자
by
Brimble, Mark A.
;
Morton, Christopher L.
;
Winston, Stephen M.
;
Reeves, Isaiah L.
;
Spence, Yunyu
, et al.
소스
Human Gene Therapy
. Jul2024, Vol. 35 Issue 13/14, p477-489. 13p.
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7 . Academic Journal
Haemophilia gene therapy: Progress and challenges
저자
by
Lheriteau, Elsa
;
Davidoff, Andrew M.
;
Nathwani, Amit C.
.
소스
In
Blood Reviews
September 2015 29(5):321-328
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5 . Academic Journal
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
저자
by
McIntosh, Jenny
;
Lenting, Peter J.
;
Rosales, Cecilia
;
Lee, Doyoung
;
Rabbanian, Samira
, et al.
소스
In
Blood
25 April 2013 121(17):3335-3344
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7 . Academic Journal
Codon optimization of human factor VIII cDNAs leads to high-level expression
저자
by
Ward, Natalie J.
;
Buckley, Suzanne M.K.
;
Waddington, Simon N.
;
VandenDriessche, Thierry
;
Chuah, Marinee K.L.
, et al.
소스
In
Blood
20 January 2011 117(3):798-807
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7 . Academic Journal
Improved Intratumoral Oxygenation Through Vascular Normalization Increases Glioma Sensitivity to Ionizing Radiation
저자
by
McGee, Mackenzie C.
;
Hamner, J. Blair
;
Williams, Regan F.
;
Rosati, Shannon F.
;
Sims, Thomas L.
, et al.
소스
In
International Journal of Radiation Oncology, Biology, Physics
2010 76(5):1537-1545
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7 . Academic Journal
Long-Term Persistence of Antibodies to Adeno-Associated Viral Vectors Following Gene Therapy with scAAV8-LP1-Fixco
저자
by
McIntosh, Jenny H.
;
Mohamed, Saira
;
Ireland, Lydia
;
Morton, Christopher L
;
Reiss, Ulrike M.
, et al.
소스
In
Blood
2 November 2023 142 Supplement 1:2255-2255
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